Reversal of established bone pathology in MPS VII mice following lentiviral-mediated gene therapy

dc.contributor.authorDerrick-Roberts, A.
dc.contributor.authorPanir, K.
dc.contributor.authorPyragius, C.
dc.contributor.authorZarrinkalam, K.
dc.contributor.authorAtkins, G.
dc.contributor.authorByers, S.
dc.date.issued2016
dc.description.abstractAbstract not available
dc.description.statementofresponsibilityAinslie L.K. Derrick-Roberts, Kavita Panir, Carmen E. Pyragius, Krystyna H. Zarrinkalam, Gerald J. Atkins, Sharon Byers
dc.identifier.citationMolecular Genetics and Metabolism, 2016; 119(3):249-257
dc.identifier.doi10.1016/j.ymgme.2016.09.003
dc.identifier.issn1096-7192
dc.identifier.issn1096-7206
dc.identifier.orcidPanir, K. [0000-0001-7139-819X]
dc.identifier.orcidAtkins, G. [0000-0002-3123-9861]
dc.identifier.orcidByers, S. [0000-0001-5576-3636]
dc.identifier.urihttp://hdl.handle.net/2440/103995
dc.language.isoen
dc.publisherElsevier
dc.relation.granthttp://purl.org/au-research/grants/nhmrc/565081
dc.rights© 2016 Elsevier Inc. All rights reserved.
dc.source.urihttps://doi.org/10.1016/j.ymgme.2016.09.003
dc.subjectMucopolysaccharidosis type VII; skeletal pathology; gene therapy; lentiviral vector micro-CT
dc.titleReversal of established bone pathology in MPS VII mice following lentiviral-mediated gene therapy
dc.typeJournal article
pubs.publication-statusPublished

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